A phase 2 study of HQK-1001, an oral fetal haemoglobin inducer, in β-thalassaemia intermedia

Adlette Inati, Mario Kahale, Susan P. Perrine, David H.K. Chui, Ali T. Taher, Suzanne Koussa, Therese Abi Nasr, Hussein A. Abbas, Richard G. Ghalie

Research output: Contribution to journalLetterpeer-review

8 Scopus citations
Original languageEnglish (US)
Pages (from-to)456-458
Number of pages3
JournalBritish Journal of Haematology
Volume164
Issue number3
DOIs
StatePublished - Feb 2014
Externally publishedYes

Keywords

  • Anaemia
  • Fetal haemoglobin
  • Gene expression
  • Haemoglobinopathies
  • β-thalassaemia

ASJC Scopus subject areas

  • Hematology

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